Nakai lab receives three NIH grants to develop potential curative treatments for inherited kidney diseases Hiroyuki Nakai, ...

Valentina Ruggeri’s parents were told their little girl was the only person in Australia with an ultra-rare genetic condition – and there was no cure. So they took matters into their own hands. But ...

Rocket Pharmaceuticals (RCKT) rose in afternoon trading on Thursday after Goldman Sachs upgraded the gene therapy developer to Neutral from Sell, citing the latest updates on RP-A501, its experimental ...

Researchers report encouraging findings from the first clinical cohort of blind people treated with optogenetic therapy ...

Prioritize viral vectors, oncology and rare disease therapies, with North America offering strong ROI potential through regulatory support, R&D investment and early adoptionDublin, Oct. 08, 2026 ...

Record global approvals, CRISPR breakthroughs, and expanding clinical and commercial activity are accelerating demand for cell and gene therapy tools and reagents.Dublin, Oct. 08, 2026 (GLOBE NEWSWIRE ...

A gene therapy makes surviving retinal ganglion cells light-sensitive, allowing blind patients to detect objects using stimulating goggles.

Researchers have demonstrated that optogenetic gene therapy can partially restore sight in blind individuals, showing promise for future high-resolution vision restoration.

Researchers at Oregon Health & Science University have been awarded more than $7.5 million in new National Institutes of ...

Optogenetics, recognized by the 2026 medicine Nobel, makes cells respond to light, including eye cells that normally relay ...

Scientists have taken another important step toward restoring vision in people with certain inherited forms of blindness. In ...