More than two years after its approval, only about 60 patients across the U.S., Middle East, and Europe have been treated ...

At age 45, Dr. Lakiea Bailey said, for the longest time, that she was the oldest person with sickle cell anemia that she knew. The executive director of the nonprofit patient advocacy group the Sickle ...

Two Pee Dee siblings are officially cured of sickle cell disease after more than a decade of living with the genetic blood ...

The Food and Drug Administration has approved the world’s first medicine based on CRISPR gene-editing technology, a groundbreaking treatment for sickle cell disease that delivers a potential cure for ...

LOS ANGELES (KABC) -- It's been more than a month since the FDA approved two milestone gene-editing treatments for sickle cell disease, but lining up patients for these therapies will be a challenge ...

UCSF Benioff Children's Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell disease. The trial is the first in the U.S. to apply non-viral CRISPR-Cas9 ...

Jason Mast is a general assignment reporter at STAT focused on the science behind new medicines and the systems and people that decide whether that science ever reaches patients. You can reach Jason ...

Gene therapy is a medical treatment that works by changing or fixing a person's genes to treat or prevent disease ...

At the weekend in Kampala, a piece of news landed that could reshape the future of one of the world’s most neglected diseases. The United States Patent and Trademark Office (USPTO) had accepted a ...

A treatment about to be tested in California holds the promise of possibly curing a debilitating disease, that disproportionately affects the African American community, sickle cell disease.

UCSF Benioff Children's Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell disease. The trial is the first in the U.S. to apply non-viral CRISPR-Cas9 ...

Patients with sickle cell disease (SCD) often face a reduced quality of life and a lower life expectancy. Allotransplantation, the first treatment for SCD with curative potential, comes with risks, ...